Tim Yu @timyu
Neuroscience, Genetics, Genomic Medicine. Tweets my own unless one of our girls has broken into my account again in which case sorry for all the Pokémon pics theyulab.org Joined July 2007-
Tweets434
-
Followers2K
-
Following325
-
Likes2K
Gene editing pioneer @davidrliu discusses baby K.J. Muldoon, the first person treated with a customized gene editing therapy, what made K.J.'s treatment possible, and how on-demand treatments for rare genetic diseases could one day become routine. broad.io/DLQA
New paper out. Thanks to @irdirc N=1 taskforce members for a very positive, proactive and pleasant collaboration @N1Collaborative @n_lorem @timyu and others! bsky.app/profile/oligog…
Privileged to be a physician-scientist in a time when efforts like these spanning genetics, engineering, & medicine come to fruition. Hats off to @kiranmusunuru, Rebecca Ahrens-Niklas ,@UrnovFyodor & more for this milestone in interventional genetics. nejm.org/doi/full/10.10…
Save the date - you're invited to attend the 21st Annual Meeting of the Oligonucleotide Therapeutics Society. This event will be held on October 19-22, 2025, at the Budapest Congress Center in Budapest, Hungary. oligotherapeutics.org #OTS25 #oligomeeting #OTS #careers
David Cheerie and I will present at the first @N1Collaborative annual meeting tomorrow! We will discuss the newly established N1C VARIANT (Variant Assessments towards Eligibility for Antisense Oligonucleotide Treatment) Guidelines. medrxiv.org/content/10.110…
Announcing Zebronkysen: Amelia & Makenzie receive personalized ASO drug. This milestone would not be possible without the incredible support of the ForeBatten community and the passionate development team. More information on this exciting news is on forebatten.org
Thanks to co-authors @roon_mom @LaufferMarlen @collinrwj @ypeelgersma The paper describes how @timyu & @stopbatten inspired us to start DCRT and lessons we have learned in our first 4 years (spoiler: most important lesson: it is important to collaborate & share @N1Collaborative)
Our paper on the DCRT is out now in @TARareDisease Joining forces to develop individualized antisense oligonucleotides for patients with brain or eye diseases: the example of the Dutch Center for RNA Therapeutics - (sagepub.com)
Join us for a webinar on July 25th at 8am PDT titled "Nucleic Acid Therapeutics: Successes, Milestones, and Upcoming Innovation." Register now: oligotherapeutics.org/nucleic-acid-t… #nucleicacidtherapeutics #biotechnology #pharmaceuticalresearch #otswebinar #ots #nucleicacid
A remarkable milestone yet buried the lede: He wants to be a geneticist. nytimes.com/2024/05/06/hea…
This Thursday April 25 from 4:00-6:30 pm at the Broad Institute Julia Vitarello (Mila's mom @stopbatten), Casey McPherson (Rose's dad @ToCureARose), @The_Termeer_Fdn, @Cookies4Cures, @broadinstitute, and others will host "Rock n' Rare", a special event of inspirational stories and music celebrating family and friends of rare disease patients, scientists, doctors, and the interested public. Stories and appearances by Julia, Casey, @timyu, @SammyBasso, Dana Perella, Cole Quinn, Weston McPherson, and myself. Music by Casey McPherson and AlphaRev. Registration: betterunite.com/rocknrare
Very happy that our recommendations for the identification of suitable variants for individualized ASO treatments are now published! Big thanks go to our PhD candidate Bianca Zardetto, @oligogirl, @roon_mom, and our colleagues from the @N1Collaborative hindawi.com/journals/humu/…
Published today, our reasons for optimism that success rates in drug discovery can be improved by picking the right targets using human genetics: nature.com/articles/s4158… I break the key findings down panel by panel in this thread: x.com/cureffi/status…
Is having even more gene-disease associations still useful for picking drug targets? For which types of programs does it matter? Has pharma shifted focus towards genetically validated targets? New paper by me, @mnelsonxy, @DongCoco90417, & @jivecast doi.org/10.1101/2023.0…👇
Montage: Totality -4 min, Totality -10 sec, Totality -5 sec, 1st min of totality, 2nd min of totality, 3rd min of totality, Totality +3 sec, Totality +5 sec, Totality +2 min
Thank you @natashaloder and The @Telegraph for sharing Mila's story and the critical role the UK is playing in proving a model for individualized medicines at scale. telegraph.co.uk/global-health/…
Our first session ‘After Mila’ with @stopbatten @UrnovFyodor @Jasonmmast #STATBreakthrough
@davidrliu @stopbatten Science & humanity🙏. Thanks my friend.
We have many excellent resources on the website from the OTS President's perspective & educational videos, to in-depth articles. View our resources on the menu under "Science News." oligotherapeutics.org #ots #oligonucleotide #biotechnology #science #sciencenews
Today is a very exciting day. The UK government announced in the Autumn Statement by Chancellor Jeremy Hunt, their support for the individualized medicines pilot MMF initiated over a year ago with support from Daniel O'Connor @parkermoss @Rich_Genomics @nicolablackwood @timyu
The first in vivo base editing clinical trial outcomes are now reported, following last year’s positive ex vivo base editing clinical outcomes! Congratulations to @kiranmusunuru , @skathire, @ambellinger, @NicoleGaudelli, & other scientists at @VerveTx and @BeamTx on these positive data.
The culmination of 10+ years of work to use #CRISPR gene editing to fight heart disease! @ambellinger @VerveTx $VERV presenting the interim data from the ongoing heart-1 Phase 1b clinical trial of VERVE-101 base editing for HeFH patients, at #AHA23 now. Let’s start! 🧵
David R. Liu @davidrliu
79K Followers 68 Following Professor at Harvard and the Broad Institute. Our lab integrates chemistry & evolution to illuminate biology & enable new therapeutics. IG/Threads: @davidrliu1
Ethan Perlstein 1-to-... @eperlste
19K Followers 2K Following ceo @1000cures, ceo @PerlaraPBC (w16 @ycombinator), founder @epalrestat, founder @endrarediseases, founder @smer28rapa
Effie Parks @OnceUponAGene
7K Followers 4K Following Rare Disease Advocate | Award Winning Podcaster | Speaker | Captain Connection | RareMama to my sweet, Ford, who lives with #CTNNB1 🦓
Joseph G. Gleeson @jogleeson_ucsd
2K Followers 146 Following #UCSD Neurogeneticist studying origins and treatments of pediatric brain disease. CMO of #NLorem, and Neuroscience Director at #RCIGM
n-Lorem Foundation @n_lorem
1K Followers 558 Following Non-profit discovering, developing, and providing personalized experimental ASO medicines to treat nano-rare patients — for free, for life
Fyodor Urnov @UrnovFyodor
34K Followers 503 Following Gene editor + Professor Molecular Therapeutics @berkeleyMCB + Director for Technology and Translation @igisci + @danahercorp Beacon for CRISPR Cures.
Veera Rajagopal @doctorveera
21K Followers 5K Following 🇮🇳 MBBS, MD, 🇩🇰 PhD | 🧬 Co-founder & CSO @wellytics Building genetics-driven drug discovery in India Thoughts: https://t.co/QKUXWuTGfr
Dr. Heather Mefford @... @hcmefford
3K Followers 882 Following Physician, scientist, mom, wife #genetics #epilepsy #pediatrics #raredisease @StJude @StJudeResearch formerly @UWMedicine
Luke Rosen @lukebrosen
2K Followers 423 Following Founder of https://t.co/GkrwXhfkoy and https://t.co/eWtcezWeJc. Firefighter. Works with families affected by neurological diseases and cancer. Baseball and hockey. Proud dad.
Clement Chow @ClementYChow
15K Followers 5K Following henfluencer - geriatric millennial - #stopasianhate - don’t call me Clem - emotional eater™️- he/him- @chowlab
Mila's Miracle @stopbatten
817 Followers 347 Following Mila fought hard against Batten disease, a rare fatal condition with no cure. Her story is now giving new hope to millions with genetic disease.
Nicole M. Gaudelli @NicoleGaudelli
6K Followers 286 Following EIR @GVteam, dreamer, inventor of ABE. Interested in genomic medicine and next-generation application of gene editing tools. Leonardo’s & Isabella’s Mom.
AnnemiekeAartsma-Rus @oligogirl
3K Followers 449 Following Translating science from bench to bedside and from jargon to lay language
FamilieSCN2A @FamilieSCN2A
2K Followers 1K Following Our vision is to find effective treatments and a cure for SCN2A disorders.
Pankaj Agrawal @AgrawalPB_lab
832 Followers 699 Following Physician-in-Chief, Holtz, @uhealth pediatrics Neonatal Chief @univmiami @jacksonhealth Prof. Pediatrics Genetics, Project Newborn Chair
Ana Mingorance @CNSdrughunter
3K Followers 1K Following 🧠 🧬 Neuroscientist. Looking for new medicines for CDKL5, SCN1A, SHANK3, DHPS and a few others. @cnsdrughunter.bsky.social
The Notorious EEG (M.... @TheNotoriousEEG
10K Followers 2K Following Epileptologist/Head of Neurosciences @cookchildrens, I 💜 #HailState, buffalo wings, art, music & foremost Becky & my daughters. Views are mine, not my employer
Sri Kosuri @srikosuri
19K Followers 3K Following Cofounder & CEO, @octantbio ; BoD @Ginkgo ; Husband of @karinlynnalm ; Previously Associate Professor, @uclachem
CACNA1A Foundation @cacna1a
2K Followers 2K Following Nonprofit dedicated to a brighter future for those with CACNA1A variants. On a mission to fund life changing research while supporting families along the way.
tea-y06k@ @TeaY06k
0 Followers 25 Following
alex rubinsteyn @iskander
7K Followers 5K Following Genomics + immunology + ML = personalized cancer immunotherapy | https://t.co/nReVwtVHPq | https://t.co/8DWibdfDWa
Felix Raimundo 🧬�... @gama_search
607 Followers 467 Following RNA is cool I guess ? CEO @tychobio_ai previously @GoogleAI and @institut_curie
Kyle Farh MD PhD - Il... @KyleFarh
392 Followers 1K Following Head of Illumina AI Lab. Deep Learning. Human Genetics. Perturb-seq.
canoebrookbl @canoebrookbl
742 Followers 668 Following
Rae 🍽️ @raechellambert
6K Followers 3K Following IRLmaxxing | Hosting parties with real dishes and powering white-labeled dinner clubs worldwide. Co-Founder of DNNR (https://t.co/fhYVRbUepQ) & building Freedom Village.
Akano Lordstrong @Grace_fuelled
211 Followers 6K Following
Wynston Arails @WArails83674
23 Followers 438 Following
Alexandra Thomas @Alex_Thomas___
13 Followers 5K Following
Abdulla Hamed Alshams... @HamedAlsha98969
181 Followers 2K Following السيد عبدالله حامد الشامسي مدير بنك دبي الإسلامي دبي الإمارات العربية المتحدة، الإمارات العربية المتحدة هي وطني، أحب بلدي، وأحاول أن أكون صادقًا مع زملائي من ا
مصمم طبي @MEDICANER
1K Followers 1K Following أساعد الأطباء والعيادات على تحويل المعلومات الطبية المعقدة إلى تصاميم بصرية جذابة ومبسطة إنفوجرافيك طبي | بوسترات أبحاث | محتوى سوشيال ميديا للطلب تواصل واتس
عبدالله الف... @Abdullah_Med
4K Followers 915 Following استشاري طب الأطفال وعلم الجينوم الطبي والجزيئي | حساب شخصي | محتوى علمي🧬 | Medical and Molecular Genomics Consultant | Married to the most amazing woman
Maya Jay @neurojaym
1K Followers 1K Following building @FlagshipPioneer 🚀 | BioxML 🧬@LilaSciences | previously @PiN_Harvard @MIT | she/her/dr, views are my own
Tim Hurley @timphurley
39 Followers 264 Following
Achanya P @AchanyaP9564
3 Followers 321 Following
Qeawer @Qeawer9518903
21 Followers 1K Following
Nozha Borjini @NBorjini
81 Followers 264 Following Scientist @IBiS_Sevilla #microglia_lovers #in_vivo_imaging
Mahesh Kumar @MKumarTweets
151 Followers 408 Following Materials Sci, Computer Science, - dad to GNAO1 warrior princess. bassist, guitarist, curiosity may have killed the cat, it keeps me going. love rule breakers
Valentin F. Cracan @VFCracan
1K Followers 2K Following Assistant professor at the Scintillon Institute. Assistant professor adjunct of Molecular and Cellular Biology at Scripps Research. Working on redox metabolism.
LMBRD2 Association @lmbrd2france
14 Followers 6 Following Association à but non lucratif qui promeut recherche scientifique et à l’aide aux familles touchées par une maladie rare liée au #LMBRD2
Prudhvi Sai @Prudhvi028
54 Followers 107 Following CIRM Stem Cell Research Intern at UCSD @jogleeson_ucsd Lab for Pediatric Brain Disease Masters Student at CSUCI
Auditor @auditor112017
306 Followers 49 Following Retired Internal Auditor (CISA), Accountant, and Info Sec Engineer. Followed biotech, pharma, banking and tech sectors for more than 25 years.
Catherine Whittinghil... @cwillingworth
380 Followers 300 Following Advocacy for CMT4C | "Sharpen here, reader, your eyes to the truth, for the veil is now surely so fine that passing within is easy." Purg. 8.19-21
kahwai @kahwai222
39 Followers 2K Following
Nicolò Tesio @nicolotesio
137 Followers 689 Following
BioBucksResearch @BioBucks33
54 Followers 715 Following
sorokingMMA @Fashionmenice35
126 Followers 1K Following NEW YORK ISLANDERS | NEW YORK METS | MMA FAN FOR LIFE | CD COLLECTOR | AUDIOPHILE
Silvia Ramundo @ramundo_silvia
3K Followers 2K Following Cell biology, genetics, biotechnology, algae & other green organisms; I study (and often torture) chloroplasts; group leader @GMIVienna @ViennaBiocenter.
Kunée @KKunee35613
194 Followers 4K Following Je peux voir l’avenir. Je suis un méta-humain. JE NE ME SUIS JAMAIS FAIT VACCINER.
yumin cheong @yumin0216
2 Followers 119 Following 🇰🇷 md candidate deeply interested in functional genomics
Jim Breyer @jimihendrixlive
24K Followers 26K Following https://t.co/f3lprY5S2e, Austin TX, venture capital/investing/venture philanthropy,conservation,Smiles and Laughter
Esra Serdaroglu @EsraSerdaroglu
1K Followers 2K Following Child neurologist interested in neuromodulation
Robert Thompson, MD @RMThompsonMD
101 Followers 127 Following Genetics & Metabolism Fellow in the Harvard Medical School Genetics Training Program / Neurogenetics and Gene Therapy Fellow at MGB. Opinions my own.
Dex Gem @DexGem__
347 Followers 3K Following Early alpha solana analyst || Precision entries || entry and exits #solana || daily 10-100x 💎 on my TG
Oligonucleotide Thera... @OTDC_2026
10 Followers 229 Following Sciinov Group welcomes you to the OTDC 2026 Conference during May 25-26, 2026, in Rome, Italy.
Journal of Translatio... @OfGenomics
508 Followers 3K Following Official account of Journal of Translational Genetics and Genomics(JTGG). Impact factor1.0, journal #golden open access #continuous #innovative
Elena Mishina @ElenaMishina15
167 Followers 1K Following Neuroscientist and Longevity Advocate | BiteLabs HealthTech'24 | @_buildspace n&w s3-s4 | @shefiorg'14 | @enter_delta Chapter II
Adult Doll Fun Doll F... @kcardosop
136 Followers 3K Following Adult Doll Factorywebsite：https://t.co/izAUCRXHGr ，https://t.co/BberyhZkJe。 WhatsApp/teregram: +86 13310819752 +86 18125735508 mailbox: [email protected]
Midhun Anne @Midhun_NK_Anne
123 Followers 820 Following Postdoc @TheFlorey | PhD from @OhioState Characterized Scn8a T767I mouse model in the Wagnon Lab | 👨🏻🔬🔬🧬🧪🧫🥼
Nourhan Mahsoub @nourhan_mahsoub
4 Followers 131 Following Founder of Octides | Biotech Researcher ✨
Rezwan Siddiquee @RezwanSidd
287 Followers 726 Following PhD Candidate | SynBio | seekRNA | IS110/IS1111 gene editing | @Sydney_Uni. https://t.co/oFsDAHAePh
Meggan Buckwell @meggbuckwell
42 Followers 288 Following
Atish @Atish70155226
0 Followers 4 Following Oligo chemist dedicated to advancing nucleic acid research
Mathepan Mahendraling... @mathepan
741 Followers 1K Following MD-PhD candidate @uoftmdphd | Researching childhood cancers | Genomics, Writing & Donut enthusiast | Learning and Unlearning
David Apple @davidcapple
2K Followers 957 Following Founder @sharktoothbio • Early @NotionHQ & @Typeform • B2B SaaS Advisor & Angel Investor • Board @cmtausa • Proud Papa of 2 👨👩👧👦 • 🇫🇷 🇺🇸
David R. Liu @davidrliu
79K Followers 68 Following Professor at Harvard and the Broad Institute. Our lab integrates chemistry & evolution to illuminate biology & enable new therapeutics. IG/Threads: @davidrliu1
Ethan Perlstein 1-to-... @eperlste
19K Followers 2K Following ceo @1000cures, ceo @PerlaraPBC (w16 @ycombinator), founder @epalrestat, founder @endrarediseases, founder @smer28rapa
Joseph G. Gleeson @jogleeson_ucsd
2K Followers 146 Following #UCSD Neurogeneticist studying origins and treatments of pediatric brain disease. CMO of #NLorem, and Neuroscience Director at #RCIGM
n-Lorem Foundation @n_lorem
1K Followers 558 Following Non-profit discovering, developing, and providing personalized experimental ASO medicines to treat nano-rare patients — for free, for life
Fyodor Urnov @UrnovFyodor
34K Followers 503 Following Gene editor + Professor Molecular Therapeutics @berkeleyMCB + Director for Technology and Translation @igisci + @danahercorp Beacon for CRISPR Cures.
Ingo Helbig @IngoHelbig
3K Followers 381 Following Child Neurologist, epilepsy genetics researcher, blogger
Dr. Heather Mefford @... @hcmefford
3K Followers 882 Following Physician, scientist, mom, wife #genetics #epilepsy #pediatrics #raredisease @StJude @StJudeResearch formerly @UWMedicine
Luke Rosen @lukebrosen
2K Followers 423 Following Founder of https://t.co/GkrwXhfkoy and https://t.co/eWtcezWeJc. Firefighter. Works with families affected by neurological diseases and cancer. Baseball and hockey. Proud dad.
Clement Chow @ClementYChow
15K Followers 5K Following henfluencer - geriatric millennial - #stopasianhate - don’t call me Clem - emotional eater™️- he/him- @chowlab
Mila's Miracle @stopbatten
817 Followers 347 Following Mila fought hard against Batten disease, a rare fatal condition with no cure. Her story is now giving new hope to millions with genetic disease.
AnnemiekeAartsma-Rus @oligogirl
3K Followers 449 Following Translating science from bench to bedside and from jargon to lay language
Michael 英泉 Eisen @mbeisen
73K Followers 13K Following I science & try to make science open. Tweets do not represent my employer's views, but are always correct. My conflicts of interest https://t.co/77P0LDe6VR.
John Maraganore 🇺�... @JMaraganore
16K Followers 423 Following Founding CEO of @Alnylam. Pioneered RNAi therapeutics as a whole new class of medicines for patients. Now bioentrepreneur-at-large. Opinions are my own.
FamilieSCN2A @FamilieSCN2A
2K Followers 1K Following Our vision is to find effective treatments and a cure for SCN2A disorders.
Mike Graglia 🌻 @JMGraglia
7K Followers 2K Following CEO @cureSYNGAP1 🧬 Pod https://t.co/9jkDkMg5R8 🎧 Alum @GonzagaU @peacecorps @pdosoros @SAISHopkins @Columbia_Biz @IFC_org @bcg @gatesfoundation @newamerica
Pankaj Agrawal @AgrawalPB_lab
832 Followers 699 Following Physician-in-Chief, Holtz, @uhealth pediatrics Neonatal Chief @univmiami @jacksonhealth Prof. Pediatrics Genetics, Project Newborn Chair
Ana Mingorance @CNSdrughunter
3K Followers 1K Following 🧠 🧬 Neuroscientist. Looking for new medicines for CDKL5, SCN1A, SHANK3, DHPS and a few others. @cnsdrughunter.bsky.social
Sri Kosuri @srikosuri
19K Followers 3K Following Cofounder & CEO, @octantbio ; BoD @Ginkgo ; Husband of @karinlynnalm ; Previously Associate Professor, @uclachem
Pradeep Natarajan @pnatarajanmd
29K Followers 802 Following Dir of Prev Cardiology @MassGeneralNews | Assoc Dir of Pers Med @MassGenBrigham | Prof @harvardmed | Assoc Mem @broadinstitute | Assoc Ed @JAMA_current
Jon Watts @jwattsgroup
938 Followers 237 Following Oligonucleotide Therapeutics and Chemical Biology. Find us also at @jwattsgroup.bsky.social
Wafik S. El-Deiry, MD... @weldeiry
22K Followers 10K Following Physician-Scientist https://t.co/8RMRruPhfx Discoverer of p21(WAF1), TRAIL Death Receptor DR5 and TIC10/ONC201 the 1st ever FDA approval for H3K27M-gliomas
Nicola Blackwood @nicolablackwood
15K Followers 3K Following Chair @GenomicsEngland, Chair @OxUInnovation, Board Member @BioNTech_Group, Former Innovation Minister, old time musician.
UK Platform for Nucle... @UpNAT_node
90 Followers 234 Following Creating a national network of experts/stakeholders to facilitate & promote the development of Nucleic Acid Therapies for patients with rare diseases in the UK
Jillian Wise,PhD @jillianmcwise
262 Followers 504 Following Cancer Immunologist and Computational Biologist, PhD. Women in Science. Travel Enthusiast. Mother. Wife.
Anastasia Khvorova @wolkhv
49 Followers 233 Following
Sammy Basso @SammyBasso
1K Followers 22 Following Lotto per la ricerca sulla Progeria e lotto per un mondo migliore
Kaitlin Samocha @ksamocha
4K Followers 617 Following Assistant Investigator @CGM_MGH. Focus on human genomics and modeling rare variation. She/her. You can find me on the other place with the same name.
Dr. Erin M. McConnell @Bluebird__47
1K Followers 2K Following (she/her) DNA nanotechnology, chemistry, and oligonucleotide therapeutics. Research Scientist in DeRosa Lab at Carleton University.
Simons Searchlight @s_searchlight
2K Followers 3K Following Accelerating research by collecting data/biosamples from ppl w/rare #genetic causes of #autism & other neurodev dis. Researchers can get data: https://t.co/kokQ7uLYWd
La Jolla Labs Inc. @lajollalabs
237 Followers 389 Following La Jolla Labs was founded by leaders in RNA therapeutics to leverage advances in automation and computing to build the world's fastest drug discovery pipeline.
Dan O'Reilly @DANorDNA
751 Followers 723 Following Postdoctoral Associate, Khvorova lab, RNA Therapeutics Institute, UMass Medical School. Ph.D. Damha lab, McGill university
Ebrahimi-Fakhari_Lab @DEF_Lab_HMS
286 Followers 442 Following Est. 2023. The Ebrahimi-Fakhari lab is committed to developing novel therapies for rare neurological diseases in children. 🧬🧠🔬 @harvardmed @BostonChildrens
Buitengebieden @buitengebieden
2.9M Followers 78 Following The official positive side of 𝕏. I’m Sander from the Netherlands. All copyrights belong to their respective owners! DM for credits/removal/submission!
LiptonLab @Lipton_Lab
109 Followers 110 Following The LiptonLab researches the interface between circadian clocks and neurological disease. Tweets are personal opinions.
Alice Chen-Plotkin @alicechenp
2K Followers 343 Following Neurologist-neuroscientist at the University of Pennsylvania. Mom (of two), wife (of one).
Tojo Nakayama @tojonakayama
5 Followers 23 Following
Brendan Frey @frey_brendan
535 Followers 6 Following
Maya Chopra @Maya__Chopra
101 Followers 117 Following Clinical Geneticist. Researcher. Uniquely global experience and perspective🇦🇺 🇨🇳 🇫🇷 🇺🇸
HogIsland @hog_island
6 Followers 151 Following
Science in Boston @ScienceinBoston
3K Followers 2K Following Your complete source for life science news and events in the Greater Boston Area. Brought to you by the Science in the City program at @STEMCELLTech.
Jim Dowling @jdowling007
181 Followers 293 Following
Elaine T Lim @elimtt
196 Followers 229 Following Human genetics and genomics. Innate Immunity. Brain organoids. Assistant professor @UMassChan
Prof. Toshi Yokota Ph... @ToshifumiYokota
5K Followers 5K Following Medical Geneticist| RNA Therapeutics Innovator| FCAHS Canadian Academy Fellow| Distinguished Professor@UAlberta| Driving innovation in genetic medicine
N1 Collaborative @N1Collaborative
133 Followers 2 Following Working together to bring individualized genetic medicines safely and rapidly to patients worldwide
Sijae Woo @SijaeW
7 Followers 69 Following
Dr Haiyan Zhou @lab_zhou
399 Followers 257 Following Trained in clinical medicine now a scientist @UniversityCollegeLondon, Prof of Genetic Medicine on translational RNA therapy .
Pauline De Graaf @GraafPauline
5 Followers 4 Following
NeuroD Lab Leiden @NeuroD_Lab_LUMC
92 Followers 65 Following Official Twitter account of the NeuroDegeneration Lab of prof. @roon_mom at the Dpt. of Human Genetics @LUMC_Leiden. Tweets by @LaurieKerkhof and @BuijsenRonald
Gulcin Gumus @gulcingumus1
571 Followers 586 Following Molecular biologist and geneticist & Research and Policy Senior Manager @eurordis Rare Diseases Europe #genomics #diagnosis #newbornscreening #patientadvocacy
Peter J Park @peter_j_park
2K Followers 112 Following professor of biomedical informatics, bioinformatics/genomics with applications to cancer and neuroscience
Tania Simoncelli @TaniaSimoncelli
505 Followers 549 Following
Pharmagellan @pharmagellan
330 Followers 1 Following Biotech consultancy focused on R&D strategy | Our 2 books on biotech clinical trials & financial modeling are both on Amazon | More tweets at @Frank_S_David
Frank S. David @Frank_S_David
8K Followers 565 Following Biotech advisor @Pharmagellan. Professor of the Practice of Biotech @tufts_biology. Lurking here; posting at @franksdavid.bsky.social.
Leway Chen, MD, MPH @DocDiastole
828 Followers 889 Following Medical Director, Advance HF Program, Professor of Medicine, University of Rochester. (Tweets are my own!). Tesla: LEWAY88279; Rivian: LEWAY16327716
Justin West @DrJustinWest
129 Followers 151 Following Dr. Justin West is the director of plastic and reconstructive surgery for Finesse Plastic Surgery in Orange County, CA.
Curedlg4 @curedlg4
65 Followers 120 Following We are a small non-profit whose central goal is to support the research and development of treatments, therapies, and support systems for individuals with DLG4
Anonymous @doc_bronc
16 Followers 324 Following
Nesrin Yasser Issa @nesrinyasser2
20 Followers 73 Following Research Specialist @Dubai Genome project Talks about # Antisense Therapeutics, # Rare genetic diseases, # long read sequencing , # scRNA-seq
Anne O'Donnell-Luria @AnneOtation
1K Followers 311 Following Rare disease researcher and clinical geneticist using massive genomic datasets to improve clinical variant interpretation & understand incomplete penetrance.
Gemma Carvill, PhD @CarvillLab
1K Followers 573 Following rare disease geneticist | epilepsy | epigenetics | iPSCs | mentor & genetics MedEd | tweets about science, lab fun & occasionally my tiny hooman
Punit Seth @oligochemist
248 Followers 149 Following Creating new oligo modifications and delivery strategies to enable RNA therapeutics - Views expressed are my own
Ronald Buijsen @BuijsenRonald
613 Followers 732 Following Scientist | RNA therapeutics | neurodegenerative disorders | repeat expansions | iPSC-based disease modeling | #DATS | #CureQ @NeuroD_Lab_LUMC 🇳🇱 | @OTSociety
Brian Wallach @bsw5020
142K Followers 3K Following Dad, husband, activist, entrepreneur, unlikely movie star, living with ALS, a currently fatal disease. #ALSisHere #SoAreWe
Joel Hirschhorn @joelhirschhorn
573 Followers 31 Following Human geneticist and pediatric endocrinologist at Boston Children's Hospital, Broad Institute, and Harvard Medical School.
Bruno Godinho @bmcruzgod
319 Followers 189 Following I play with RNA molecules for a living, and I like it!Trends for United States
You might like
